A pioneering genetic treatment is saving lives where chemotherapy failed, offering new hope for children and adults with ...
Oliver has an inherited condition called Hunter syndrome, which causes progressive damage to the body and brain.
Please refer to the ASH 2025 online program for full session details and visit the Genetix booth (#1261) onsite.
Treating our first patient is a proud moment for Abeona and a testament to the tireless resolve of our team,” said Vish ...
Pharmaceutical Technology on MSN
Cell and gene therapy investment strategy pivots as funding dries up
Later-stage financing deals for cell and gene therapy companies reflects a broader derisking trend in the pharma industry.
Operational real-world data analyzed from patients prescribed ZYNTEGLO™ and LYFGENIA™Data demonstrates the value proposition of one-time, durable gene therapy for the treatment of sickle cell disease ...
2025 FEB 06 (NewsRx) -- By a News Reporter-Staff News Editor at Gene Therapy Daily News-- Researchers detail new data in Biotechnology - Gene Therapy. According to news reporting originating in Boston ...
The CVCT Forum is an annual, invite-only workshop that aims to cultivate a multi-stakeholder exchange to enhance clinical trials, streamline regulatory approval processes, and facilitate the ...
Investor optimism has waned as final minutes from uniQure’s pre-BLA meeting with the FDA convey that data from the company’s ...
Hemophilia gene therapies arrived a few years ago with blockbuster expectations. But now, one therapy has been pulled from ...
The cell and gene therapy (CGT) sector is undergoing a transition as companies navigate a more selective and strategy-driven ...
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